Julian Thalhammer (Avtor),
Gerhard Kindle (Avtor),
Alexandra Nieters (Avtor),
Stephan Rusch (Avtor),
Mikko R. J. Seppänen (Avtor),
Alain Fischer (Avtor),
Bodo Grimbacher (Avtor),
David Edgar (Avtor),
Matthew Buckland (Avtor),
Nizar Mahlaoui (Avtor),
Peter Kopač (Sodelavec pri raziskavi)
Povzetek
Background. Inborn errors of immunity (IEI) are rare diseases, which makes diagnosis a challenge. A better description of the initial presenting manifestations should improve awareness and avoid diagnostic delay. Although increased infection susceptibility is a well-known initial IEI manifestation, less is known about the frequency of other presenting manifestations. Objective. We sought to analyze age-related initial presenting manifestations of IEI including different IEI disease cohorts. Methods. We analyzed data on 16,486 patients of the European Society for Immunodeficiencies Registry. Patients with autoinflammatory diseases were excluded because of the limited number registered. Results. Overall, 68% of patients initially presented with infections only, 9% with immune dysregulation only, and 9% with a combination of both. Syndromic features were the presenting feature in 12%, 4% had laboratory abnormalities only, 1.5% were diagnosed because of family history only, and 0.8% presented with malignancy. Two-third of patients with IEI presented before the age of 6 years, but a quarter of patients developed initial symptoms only as adults. Immune dysregulation was most frequently recognized as an initial IEI manifestation between age 6 and 25 years, with male predominance until age 10 years, shifting to female predominance after age 40 years. Infections were most prevalent as a first manifestation in patients presenting after age 30 years. Conclusions. An exclusive focus on infection-centered warning signs would have missed around 25% of patients with IEI who initially present with other manifestations.
Ključne besede
prirojene okvare imunosti;primarne imunske pomanjkljivosti;imunska disregulacija;inborn error of immunity;primary immunodeficiency;immune dysregulation;
Podatki
Jezik: |
Angleški jezik |
Leto izida: |
2021 |
Tipologija: |
1.01 - Izvirni znanstveni članek |
Založnik: |
Elsevier |
UDK: |
616-097 |
COBISS: |
64144899
|
ISSN: |
1097-6825 |
Št. ogledov: |
522 |
Št. prenosov: |
91 |
Ocena: |
0 (0 glasov) |
Metapodatki: |
|
Ostali podatki
Sekundarne ključne besede: |
Immunity;Autoimmune diseases;Inflammation;Signs and symptoms;Registries;Imunost;Avtoimunske bolezni;Vnetje;Znaki in simptomi;Registri; |
Komentar vira: |
Nasl. z nasl. zaslona;
Član delovne skupine iz Slovenije: Peter Kopač;
Opis vira z dne 21. 5. 2021;
|
Strani: |
str. 1332-1341.e5 |
Letnik: |
ǂVol. ǂ148 |
Zvezek: |
ǂiss. ǂ5 |
Čas izdaje: |
Nov. 2021 |
DOI: |
10.1016/j.jaci.2021.04.015 |
ID: |
12954434 |